They are disorders amenable to one-time curative treatment, diseases requiring long term or lifelong treatment having relatively lower cost of treatment and diseases for which definitive treatment is available but challenges are to make optimal patient selection for benefit, very high cost and lifelong therapy, like Lysosomal Storage Disorders (LSD) like Gaucher Disease, Hunter Syndrome and Fabry Disease.They are disorders amenable to one-time curative treatment, diseases requiring long term or lifelong treatment having relatively lower cost of treatment and diseases for which definitive treatment is available but challenges are to make optimal patient selection for benefit, very high cost and lifelong therapy, like Lysosomal Storage Disorders (LSD) like Gaucher Disease, Hunter Syndrome and Fabry Disease.Read More
